- Eradicating spinal muscular atrophy by promoting and supporting research
- Helping families cope with SMA through informational programs and support
- Educating the public and professional community about SMA.
Since its inception in 1984, Families of SMA has become the largest private funder of SMA research and hosts the premier scientific SMA research meeting each year. It has over 13000 members and 22 Chapters worldwide.
Families of SMA is honored to be among the world organizations which make up the IASMA.